Awarded Grants

The ODC offers over 50 grant opportunities in 30+ disease areas annually to researchers across the globe, as well as within the Penn and CHOP communities. Since 2011, our grant programs have funded $17.2 million in rare disease research.

See below for a complete list of ODC-awarded grants since 2011. 

Full list of CDKL5 Program of Excellence Awardees

Awarded Grants

Displaying Results 141 - 150 of 175

Awardee Project Title Institution Grant Amount Funding Year
Magi Casal, Dr med vet, PhD, Dipl. ECAR Cognitive Studies in Dogs Affected with Mucopolysaccharidosis Type I (MPS I) After Intrathecal (IT) Therapy with AAV Vectors University of Pennsylvania MPS I $165,000 2014
Maria Fuller Oral fatty acid supplementation as an adjunct therapy for MPS I SA Pathology (University of Southern Australia) MPS I $301,746 2014
Dolan Sondhi, PhD Assessment of three routes of delivery of the IDUA gene (gene implicated in MPS-I) in non-human primates comparing two serotypes, AAV9 and AAVrh.10 for the treatment of MPS-I. Cornell University MPS I $225,000 2014
Aristotelis Astreinidis, PhD Evaluation of PLK1 inhibitors in a pre-clinical LAM animal model Texas Tech University Health Sciences Center MDBR - LAM $60,000 2014
Susan Slaugenhaupt, PhD Targeting miR-155 as a therapy for mucolipidosis IV Massachusetts General Hospital MDBR - ML4 $50,000 2014
Diva De Leon, MD, MSCE Pilot Study of the Efficacy and Safety of Sirolimus in the Treatment of Congenital Hyperinsulinism Children's Hospital of Philadelphia MDBR - CHI $60,000 2014
Florian Eichler, MD Adeno-associated virus serotype 9-mediated gene therapy for Adrenomyeloneuropathy Massachusetts General Hospital MDBR - ALD $50,000 2014
Maria Kontaridis, PhD Delineating the cause of gastrointestinal abnormalities in RASopathy disorders using human inducible pluripotent stem cells (iPSCs) Beth Israel Deaconess Medical Center/Harvard Medical School MDBR - RASopathies $65,000 2014
Pam Van Ry, PhD Galectin-1 protein therapy for the treatment for Laminin alpha2 related Congenital Muscular Dystrophy University of Nevada School of Medicine MDBR - CMD $35,000 2014
Chutikarn Butkinaree, PhD The Molecular Mechanisms of PCSK9-induced LDLR Degradation Clinical Research Institute of Montreal MDBR - FH $35,000 2014