Awarded Grants

The ODC offers over 50 grant opportunities in 30+ disease areas annually to researchers across the globe, as well as within the Penn and CHOP communities. Since 2011, our grant programs have funded $17.2 million in rare disease research.

See below for a complete list of ODC-awarded grants since 2011. 

Full list of CDKL5 Program of Excellence Awardees

Awarded Grants

Displaying Results 161 - 170 of 175

Awardee Project Title Institution Grant Amount Funding Year
John McKew, PhD Phenotypic screening to identify lead compounds that reduce lysosomal storage in neuronal cells derived from MPS I patients National Institutes of Health MPS I $150,000 2013
Anthony Stevens Ex vivo and in vivo assessment of next generation enzyme replacement therapies Amicus Therapeutics MPS I $134,200 2013
Charles Vite, DVM, PhD, BS Antemortem 3D EPSI metabolic mapping of the canine MPS I brain University of Pennsylvania MPS I $150,000 2013
Jeffrey Esko, PhD Intranasal Enzyme Replacement Therapy for the Brain University of California San Diego MPS I $165,000 2013
Jakub Tolar, MD Intranasal Delivery of Human IDUA University of Minnesota MPS I $330,000 2012
Jeffrey Esko, PhD Novel Transporters for MPS I Enzyme Replacement Therapy University of California, San Diego MPS I $330,000 2012
Ronald Crystal, MD Adeno-associated Virus-mediated Gene Transfer for the Treatment the CNS Manifestations of MPS I Weill Medical College of Cornell University MPS I $330,000 2012
Katherine Ponder, MD and Mark Haskins, BA, VMD, MS, PhD The Pathophysiology and the Effect of Treatments on Cardiovascular disease in Mucopolysaccharidosis I in Dogs University of Washington, St. Louis and University of Pennsylvania MPS I $330,000 2012
Calogera Simonaro, PhD and Mark Haskins, BA, VMD, MS, PhD Pre-clinical Evaluation of TNF- Antagonists for the Treatment of MPS I in Combination With Enzyme Replacement Therapy Mount Sinai School of Medicine and University of Pennsylvania MPS I $329,604 2012
Adrian Krainer, PhD Inhibiting NMD of Mutant IDUA mRNA for MPS I Therapy Cold Spring Harbor Laboratory MPS I $315,000 2012