Awarded Grants

The ODC offers over 50 grant opportunities in 30+ disease areas annually to researchers across the globe, as well as within the Penn and CHOP communities. Since 2011, our grant programs have funded $17.2 million in rare disease research.

See below for a complete list of ODC-awarded grants since 2011.

Click HERE for the full list of 2019 Million Dollar Bike Ride Pilot Grant Awardees!

Awarded Grants

Displaying Results 21 - 30 of 254

Awardee Project Title Institution Grant Amount Funding Year
Albert Misko A Prospective Natural History Study of Mucolipidosis type 4 Massachusetts General Hospital MDBR - ML4 $78,538 2020
Andrea Ballabio A comparative and quantitative approach to study lysosomal dysfunction in Mucopolysaccharidoses diseases Fondazione Telethon, TIGEM MDBR - MPS $64,063 2020
Rebecca Ahrens-Nicklas Can we improve neurologic and psychiatric outcomes in MSUD? Studies in a new mouse model The Children's Hospital of Philadelphia / The University of Pennsylvania MDBR - MSUD $44,037 2020
Ehud Gazit A novel approach for identification of therapeutic leads to the Maple Syrup Urine Disease Tel Aviv University MDBR - MSUD $44,037 2020
Paul Lockhart Development of novel human stem cell models of Beta-Propeller Protein- Associated Neurodegeneration (BPAN) for disease modelling and drug screening Murdoch Children's Research Institute MDBR - NBIA(BPAN) $61,245 2020
Lisa Young Genetic Mechanisms in Neuroendocrine cell Hyperplasia of Infancy (NEHI) The Children's Hospital of Philadelphia MDBR - NEHI $60,989 2020
Mark Schultz Testing Niemann-Pick C proteostasis therapeutics on human iPSC derived neurons Regents of the University of Michigan MDBR - NPC $61,637 2020
Marni Falk Pre-clinical animal model and cell evaluation of candidate therapies for human NUBPL disease. Children's Hospital of Philadelphia and University of Pennsylvania MDBR - NUBPL $61,134 2020
Andrew Kennedy Tissue-specific and temporal reinstatement of Tcf4 to treat Pitt-Hopkins Syndrome Bates College MDBR - Pitt Hopkins $68,709 2020
Gregor Andelfinger MEK inhibition for RASopathy associated hypertrophic cardiomyopathy CHU Sainte Justine Research Center, Université de Montréal MDBR - RASopathies $59,220 2020
1 2 3 4 5 6 26