Awarded Grants

The ODC offers over 50 grant opportunities in 30+ disease areas annually to researchers across the globe, as well as within the Penn and CHOP communities. Since 2011, our grant programs have funded $17.2 million in rare disease research.

See below for a complete list of ODC-awarded grants since 2011. 

Full list of CDKL5 Program of Excellence Awardees

Awarded Grants

Displaying Results 61 - 70 of 175

Awardee Project Title Institution Grant Amount Funding Year
Michael Green, MD, PhD Pharmacological Reactivation of the Xi-Linked CDKL5 Gene as a Potential Treatment for CDKL5 Deficiency University of Massachusetts Medical School CDKL5 $300,000 2017
Igor Nestrasil, MD Discovery of brain MRI signatures in infants with severe form of MPS I in the pre-HSCT and post-HSCT stage University of Minnesota MPS I $330,543 2017
William Peranteau, MD In utero gene editing for the correction of rare congenital diseases University of Pennsylvania Genome Editing $110,000 2016
Tejvir Khurana, MD, PhD Utrophin Genome Editing for Duchenne's Muscular Dystrophy (DMD) Therapy University of Pennsylvania Genome Editing $100,000 2016
Amanda Ackerman, MD, PhD Repair of Gene Defects in Beta-Cells from Children with Congenital Hyperinsulinism Children's Hospital of Philadelphia Genome Editing $110,000 2016
Drew Weissman, MD, PhD Nucleoside modified mRNA therapy for MPS I University of Pennsylvania MPS I $165,000 2016
Lili Wang, PhD Gene correction by AAV-CRISPR-Cas9 in the neonatal liver of mucopolysaccharidosis type I (MPS I) mouse University of Pennsylvania MPS I $330,000 2016
Charlotte Kilstrup-Nielsen, PhD Predictive Drug Repurposing for CDKL5 Syndrome University of Insubria CDKL5 $150,000 2016
Roy Perlis, MD Precision Medicine Program for CDKL5 Disorders: Therapeutic Screening Using Human iPSC Models Harvard Medical School CDKL5 $150,000 2016
Joe Zhou, PhD Identifying a Neural Circuit Readout for CDKL5 Disorder University of Pennsylvania CDKL5 $150,000 2016
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