Gene therapy’s new hope: A neuron-targeting virus is saving infant lives

November 01, 2017

CENTREVILLE, VIRGINIA—Nothing unusual jumps out upon meeting Evelyn, a bubbly almost-3-year-old with red curls—except that she should not be here, chatting with a visitor in her family’s living room, twirling in her tights to the Pharrell Williams song “Happy.”

April 08, 2015

REGENXBIO Licenses Key Technologies from UPenn for the Development of Treatments for MPS I and MPS II


Read More
Gene therapy is in Philadelphia's DNA

March 27, 2015

Gene therapy is in Philadelphia's DNA


Read More

March 19, 2015

Penn and PTC Therapeutics team up to research rare diseases


Read More

March 04, 2015

Gene Therapy's Potential Pricing Problem


Read More

March 03, 2015

Philadelphia Magazine: Spring Charity Bike Rides to Have on Your Radar


Read More

February 27, 2015

Philly.com: World Rare Disease Day: A call for earlier diagnosis and treatment


Read More

February 13, 2015

Penn Orphan Disease Center Announces First Grant Recipients from Million Dollar Bike Ride


Read More

February 06, 2015

Focus on Rare Diseases is Common at Penn Medicine


Read More
Previous
1 3 4 5 6 7
Next