Testing the efficacy of new pharmaceutical candidates for APBD

MDBRAPBD

Feb 1

Written By Million Dollar Bike Ride

Awardee: Or Kakhlon

Institution: Research Fund of the Hadassah Medical Organization

Award Amount: $52,509

MDBRAPBD2019

Million Dollar Bike Ride

What are the functional consequences of CDKL5 dysfunction in human neuronal cells?

Gene Therapy for Adult Polyglucosan Body Disease (APBD)