The use of a patient-centric neuronal cell model of Beta-Propeller Protein-Associated Neurodegeneration (BPAN) as a platform to develop novel therapies

MDBRBPAN
Written By Million Dollar Bike Ride

Awardee: Robin Ketteler

Institution: UCL MRC Laboratory for Molecular Cell Biology

Award Amount: $51,020

Funding Period: February 1, 2019 - January 31, 2020

Million Dollar Bike Ride
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Small molecule modulators of telomerase as novel treatments for dyskeratosis congenita
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Mechanistic study of WDR45/45B and their binding partner ATG2 in the autophagy pathway of neural cells