Awarded Grants

The ODC offers over 50 grant opportunities in 30+ disease areas annually to researchers across the globe, as well as within the Penn and CHOP communities. Since 2011, our grant programs have funded $17.2 million in rare disease research.

See below for a complete list of ODC-awarded grants since 2011. 

Full list of 2018 MDBR Awardees

Awarded Grants

Displaying Results 71 - 80 of 168

Awardee Project Title Institution Grant Amount Funding Year
Joe Zhou, PhD Identifying a Neural Circuit Readout for CDKL5 Disorder University of Pennsylvania CDKL5 $150,000 2016
Silvana Zanlungo Impact on Niemann-Pick C disease of the cross-talk between the c-Abl and the TFEB signaling pathways Pontificia Universidad Católica de Chile MDBR - NPC $51,000 2016
William Peranteau, MD In utero gene editing for the correction of rare congenital diseases University of Pennsylvania Genome Editing $110,000 2016
Joseph Rutkowski, PhD Inducible lymphatic hyperplasia to drive chylous accumulation mimicking lymphangiomatosis Texas A&M Health Science Center MDBR - GLA/GSD $51,000 2015
Adrian Krainer, PhD Inhibiting NMD of Mutant IDUA mRNA for MPS I Therapy Cold Spring Harbor Laboratory MPS I $315,000 2012
Elisabetta Ciani, PhD Innovative Strategy to Enhance the Efficiency of Gene Therapy for CDKL5 Disorder University of Bologna CDKL5 $118,175 2017
Raymond Wang, MD Intraarticular Gene Therapy for Canine Mucopolysaccharidosis Type I Joint Disease CHOC Children's Hospital MPS I $328,923 2017
Jakub Tolar, MD Intranasal Delivery of Human IDUA University of Minnesota MPS I $330,000 2012
Jeffrey Esko, PhD Intranasal Enzyme Replacement Therapy for the Brain University of California San Diego MPS I $165,000 2013
David Bedwell, PhD and Kim Keeling, PhD Investigating Suppression Therapy to Treat MPS I-H University of Alabama at Birmingham MPS I $330,000 2012
1 6 7 8 9 10 17