Optimizing Delivery and Endpoints of an AAV9-mediated Gene Therapy Trial in AMN

2015ALD

Jan 1

Written By Million Dollar Bike Ride

Awardee: Florian Eichler

Institution: Massachusetts General Hospital, Harvard Medical School

Award Amount: $50,000

Funding Period: January 1, 2016 - December 31, 2016

MDBR2015ALD

Million Dollar Bike Ride

Development of next-gen animal models for fibrous dysplasia (FD)/McCune-Albright syndrome (MAS)

Towards Precision Medicine in the Treatment of Congenital Hyperinsulinism in Infancy