Adaptive Optics imaging in follow-ups of choroideremia patients after gene therapy

MDBRCHM

Feb 1

Written By Million Dollar Bike Ride

Awardee: Katarina Stingl

Insitutional: University Eye Hospital Tübingen, Germany

Awarded Amount: $61,079

MDBRCHM

Million Dollar Bike Ride

Testing Niemann-Pick C proteostasis therapeutics on human iPSC derived neurons

A novel approach for identification of therapeutic leads to the Maple Syrup Urine Disease