Tissue-specific and temporal reinstatement of Tcf4 function to treat Pitt-Hopkins Syndrome

MDBRPitt Hopkins

Feb 1

Written By Million Dollar Bike Ride

Awardee: Andrew Kennedy

Institution: Bates College

Award Amount: $51,242

Funding Period: February 1, 2019 - January 31, 2020

MDBRPitt Hopkins2018

Million Dollar Bike Ride

In vitro differentiation of parathyroid cells from stem cells

Pilot study to develop a small molecule activator of TCF4 as a treatment for Pitt-Hopkins syndrome