Patient-Derived Phenotypic Assay to Discover Treatments for Tay-Sachs Disease

Awardee: Marlene Jacobson

Institution: Temple University School of Pharmacy

Award Amount: $43,000

Funding Period: January 1, 2016 - December 31, 2016

Quantitative description of the clinical course of Canavan disease

Awardee: Annette Bley

Institution: University Medical Center Hamburg-Eppendorf, Dept of Pediatrics

Award Amount: $35,000

Funding Period: January 1, 2015 - December 31, 2015