A Prospective Natural History Study of Mucolipidosis type 4

MDBRML4

Feb 1

Written By Million Dollar Bike Ride

Awardee: Albert Misko

Institution: Massachusetts General Hospital

Award Amount: $78,538

MDBRML42019

Million Dollar Bike Ride

Engineered microvessels derived from human lymphatic endothelium as an in vitro model for drug repurposing for lymphatic malformations

A comparative and quantitative approach to study lysosomal dysfunction in Mucopolysaccharidoses diseases