ASO therapy in CDKL5 deficiency disorder

CDKL5 Pilot Grant Programme2021CDKL5

May 1

Written By Million Dollar Bike Ride

Awardee: Michela Fagiolini, PhD

Institution: Boston Children's Hospital

Award Amount: $150,000

Funding Period: May 1, 2021 - April 31, 2022

CDKL52021

Million Dollar Bike Ride

EXPLOITING NEURONS- AND BRAIN-DERIVED EXOSOMES AS BIOMARKER FOR CDKL5 DEFICIENCY DISORDER

Comparison of Brain Biodistribution of Two CDKL5 Gene Therapy Vector Leads