Awarded Grants

The ODC offers over 50 grant opportunities in 30+ disease areas annually to researchers across the globe, as well as within the Penn and CHOP communities. Since 2011, our grant programs have funded $17.2 million in rare disease research.

See below for a complete list of ODC-awarded grants since 2011.

Click HERE for the full list of 2020 CDKL5 Pilot Grant Programme

Awarded Grants

Displaying Results 41 - 50 of 262

Awardee Project Title Institution Grant Amount Funding Year
Ehud Gazit A novel approach for identification of therapeutic leads to the Maple Syrup Urine Disease Tel Aviv University MDBR - MSUD $44,037 2020
Katarina Stingl Adaptive Optics imaging in follow-ups of choroideremia patients after gene therapy University Eye Hospital Tübingen, Germany MDBR - CHM $61,079 2020
Mark Schultz Testing Niemann-Pick C proteostasis therapeutics on human iPSC derived neurons Regents of the University of Michigan MDBR - NPC $61,637 2020
Konstantin Petrukhin Targeting retinoid traffic for treatment of CRB1-CRUMB1 degenerative retinal disorders Columbia University Medical Center MDBR - CRB1 $40,177 2020
Rene Maehr Developing human pluripotent stem cells for investigation and treatment of hypoparathyroidism University of Massachusetts Medical School Hypoparathyroidism Stem Cell Consortium Pilot Grant Program $500000 2019
Dr. Michael Mannstadt In vitro differentiation of parathyroid cells from stem cells Massachusetts General Hospital and Harvard University Hypoparathyroidism Stem Cell Consortium Pilot Grant Program $500000 2019
Jamie Fitzgerald, PhD A novel RNA-based CRISPR strategy for treating congenital muscular dystrophy Henry Ford Health System MDBR - Congenital Muscular Dystrophy $50,699 2019
Brian Bigger, PhD Targeted stem cell gene therapy for severe Mucopolysaccharidosis I (Hurler) University of Manchester MPS I Pilot Grant Program $165,000 2019
Natalia Gomez-Ospina, MD Optimizing cell selection and conditioning regimens for autologous transplantation of human genome-edited hematopoietic stem cells to treat MSPI Stanford University MPS I Pilot Grant Program $165,000 2019
Juliette Hordeaux, DVM, PhD Engineering AAV vector genome to evade immune responses and associated toxicity after intrathecal AAV gene therapy University of Pennsylvania MPS I Pilot Grant Program $165,000 2019
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